Search for Clinical Trial Results
DNA Repair-Deficiency Disorders - 25 Studies Found
Status | Study |
Active, not recruiting |
Study Name: Autologous Transplant of EFS-ADA Modified Bone Marrow Cells for ADA-Deficient Severe Combined Immunodeficiency (SCID) Condition: ADA-SCID Date: 2013-05-07 Interventions: Genetic: EFS-ADA transduced CD34+ cells from the bone marrow Eligible subjects will undergo bone marrow |
Terminated |
Study Name: Hematopoietic Stem Cell Transplantation (HSCT) for Children With SCID Utilizing Alemtuzumab, Plerixafor & Filgrastim Condition: Severe Combined Immunodeficiency Date: 2010-08-09 Interventions:
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Terminated |
Study Name: rAd-p53 Gene Therapy for Advanced Oral and Maxillofacial Malignant Tumors Condition: Advanced Oral and Maxillofacial Malignant Tumors Date: 2009-05-11 Interventions:
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Completed |
Study Name: MND-ADA Transduction of CD34+ Cells From Children With ADA-SCID Condition: Severe Combined Immunodeficiency Date: 2008-11-19 Interventions: Biological: ADA gene transfer Autologous CD34+ cells transduced with the retroviral vector MND-ADA, carr |
Completed |
Study Name: Gene Therapy for ADA-SCID Condition: Severe Combined Immunodeficiency Syndrome Date: 2008-01-08 Interventions: Genetic: gene transduced PBL and/or gene transduced HSC infusions of autologous PBL and/or HSC transduce |
Completed |
Study Name: Transplantation of Hematopoietic Cells in Children With Severe Combined Immunodeficiency Syndrome Condition: Severe Combined Immunodeficiency Date: 2005-09-07 Interventions:
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Recruiting |
Study Name: Genetic Basis of Immunodeficiency Condition: Severe Combined Immunodeficiency Date: 2003-02-20 |
Completed |
Study Name: Gene Transfer Therapy for Severe Combined Immunodeficieny Disease (SCID) Due to Adenosine Deaminase (ADA) Deficiency Condition: Severe Combined Immunodeficiency Syndrome Date: 2001-06-27 Interventions: Drug: CD34+ cells transduced with ADA retrovir |
Completed |
Study Name: Gene Transfer Therapy for Severe Combined Immunodeficieny Disease (SCID) Due to Adenosine Deaminase (ADA) Deficiency: A Natural History Study Condition: Severe Combined Immunodeficiency Date: 1999-11-03 Interventions:
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Completed |
Study Name: Pilot Study of Etanercept (Enbrel) in Children With Fanconi Anemia Condition: Fanconi Anemia Date: 2009-08-24 Interventions: Drug: Etanercept All qualified subjects receive 24 weekly subcutaneous injections of Etanercept. |